15.07.2013
- Buying Alexion Pharmaceuticals would help Roche make a splash in the newly lucrative area of rare or so-called orphan diseases, but it could command a price that the Swiss...
09.01.2013
- BioMarin Pharmaceutical, which makes high-priced drugs used to treat rare diseases, would not consider a buy-out offer for even a 25-30% premium, according to the company's chief...
03.01.2013
- Rare diseases are a growing focus for drug companies, with prices for some treatments for ultra-rare conditions running into hundreds of thousands of dollars a year. The following...
03.01.2013
- The Western world's first drug to fix faulty genes promises to transform the lives of patients with an ultra-rare disease that clogs their blood with fat. The only snag is the...
